Retinal gene therapy : methods and protocols /

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Bibliographic Details
Imprint:New York, NY : Humana Press : Springer, [2018]
©2018
Description:1 online resource (xvi, 380 pages) : illustrations (some color)
Language:English
Series:Methods in molecular biology ; v. 1715
Methods in molecular biology (Clifton, N.J.) ; v. 1715.
Subject:
Format: E-Resource Book
URL for this record:http://pi.lib.uchicago.edu/1001/cat/bib/11389354
Hidden Bibliographic Details
Other authors / contributors:Boon, Camiel J. F., editor.
Wijnholds, Jan, editor.
ISBN:9781493975228
1493975226
9781493975211
1493975218
Digital file characteristics:text file PDF
Notes:Includes bibliographical references and index.
Online resource; title from PDF title pate (SpringerProtocol, viewed December 5, 2017).
Other form:Print version: Retinal gene therapy . New York: Springer, 2018 9781493975211

MARC

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505 0 0 |t Small scale production of recombinant adeno-associated viral vectors for gene delivery to the nervous system /  |r Joost Verhaagen, Barbara Hobo, Erich M.E. Ehlert, Ruben Eggers, Joanna A. Korecka, Stefan A. Hoyng, Callan L. Attwell, Alan R. Harvey, and Matthew R.J. Mason --  |t Small and micro-scale recombinant adeno-associated virus production and purification for ocular gene therapy applications /  |r Christopher A. Reid and Daniel M. Lipinski --  |t Design and development of AAV-based gene supplementation therapies for achromatopsia and retinitis pigmentosa /  |r Christian Schön, Elvir Becirovic, Martin Biel, and Stylianos Michalakis --  |t Development of multigenic lentiviral vectors for cell-specific expression of antiangiogenic miRNAs and protein factors /  |r Anne Louise Askou and Thomas J. Corydon --  |t Design and in vitro use of antisense oligonucleotides to correct pre-mRNA splicing defects in inherited retinal dystrophies /  |r Alejandro Garanto and Rob W.J. Collin --  |t Three-dimensional co-culture bioassay for screening of retinal gene delivery systems /  |r Ding Wen Chen, Kathleen Pauloff, and Marianna Foldvari --  |t Retinal gene therapy for choroideremia : in vitro testing for gene augmentation using an adeno-associated viral (AAV) vector /  |r Maria I. Patrício and Robert E. MacLaren --  |t In vivo electroporation of developing mouse retina /  |r Jimmy de Melo and Seth Blackshaw --  |t Methods for in vivo CRISPR/Cas editing of the adult murine retina /  |r Sandy S. Hung, Fan Li, Jiang-Hui Wang, Anna E. King, Bang V. Bui, Guei-Sheung Liu, and Alex W. Hewitt --  |t AAV gene augmentation therapy for CRB1-associated retinitis pigmentosa /  |r C. Henrique Alves and Jan Wijnholds --  |t Dual AAV vectors for stargardt disease /  |r Ivana Trapani--  |t Optogenetic retinal gene therapy with the light gated GPCR vertebrate rhodopsin /  |r Benjamin M. Gaub, Michael H. Berry, Meike Visel, Amy Holt, Ehud Y. Isacoff, and John G. Flannery --  |t CRISPR repair reveals causative mutation in a preclinical model of retinitis pigmentosa : a brief methodology /  |r Wen-Hsuan Wu, Yi-Ting Tsai, Sally Justus, Galaxy Y. Cho, Jesse D. Sengillo, Yu Xu, Thiago Cabral, Chyuan-Sheng Lin, Alexander G. Bassuk, Vinit B. Mahajan, and Stephen H. Tsang --  |t In-depth functional analysis of rodents by full-field electroretinography /  |r Vithiyanjali Sothilingam, Regine Mühlfriedel, Naoyuki Tanimoto, and Mathias W. Seeliger --  |t Advanced ocular injection techniques for therapy approaches /  |r Regine Mühlfriedel, Marina Garcia Garrido, Christine Wallrapp, and Mathias W. Seeliger --  |t Neutralizing antibodies against adeno-associated virus (AAV) : measurement and influence on retinal gene delivery /  |r Mélissa Desrosiers and Deniz Dalkara --  |t Screening for neutralizing antibodies against natural and engineered AAV capsids in nonhuman primate retinas /  |r Timothy P. Day, Leah C. Byrne, John G. Flannery, and David V. Schaffer --  |t Subretinal and intravitreal retinal injections in monkeys /  |r Daniyar Dauletbekov, K. Ulrich Bartz-Schmidt, and M. Dominik Fischer --  |t Production of iPS-derived human retinal organoids for use in transgene expression assays /  |r Peter M. Quinn, Thilo M. Buck, Charlotte Ohonin, Harald M.M. Mikkers, and Jan Wijnholds --  |t AAV serotype testing on cultured human donor retinal explants /  |r Thilo M. Buck, Lucie P. Pellissier, Rogier M. Vos, Elon H.C. van Dijk, Camiel J.F. Boon, and Jan Wijnholds --  |t Human retinal explant culture for ex vivo validation of AAV gene therapy /  |r Harry O. Orlans, Thomas L. Edwards, Samantha R. De Silva, Maria I. Patrício, and Robert E. MacLaren --  |t Visual acuity testing before and after intravitreal injection of rAAV2-ND4 in patients /  |r Bin Li and Chenmian Wu --  |t Recording and analysis of the human clinical electroretinogram /  |r Mathieu Gauvin, Allison L. Dorfman, and Pierre Lachapelle --  |t Recording and analysis of goldmann kinetic visual fields /  |r Mays Talib, Gislin Dagnelie, and Camiel J.F. Boon --  |t Measuring central retinal sensitivity using microperimetry /  |r Mays Talib, Jasleen K. Jolly, and Camiel J.F. Boon --  |t Inspection of the human retina by optical coherence tomography /  |r Thomas Theelen and Michel M. Teussink --  |t Vector shedding and immunogenicity sampling for retinal gene therapy /  |r Alun R. Barnard, Anna N. Rudenko, and Robert E. MacLaren. 
650 0 |a Retina.  |0 http://id.loc.gov/authorities/subjects/sh85113322 
650 0 |a Gene therapy.  |0 http://id.loc.gov/authorities/subjects/sh85053738 
650 0 |a Genetic therapy 
650 2 |a Retina. 
650 2 |a Genetic Therapy  |x methods. 
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650 7 |a Retina.  |2 fast  |0 (OCoLC)fst01096191 
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700 1 |a Boon, Camiel J. F.,  |e editor. 
700 1 |a Wijnholds, Jan,  |e editor. 
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