In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders.

In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders.

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Bibliographic Details
Author / Creator:	Houria Bachtarzi.
Imprint:	InTech 2019.
Description:	1 online resource
Language:	English
Subject:	Genetics. Gene therapy. Medical genetics. Genetics Genetics, Medical Gene therapy Genetics Medical genetics
Format:	E-Resource Book
URL for this record:	http://pi.lib.uchicago.edu/1001/cat/bib/13438552

Hidden Bibliographic Details
ISBN:	9781789857177 1789857171 9781789857184 178985718X 9781839620829 183962082X
Summary:	Ongoing advances in pharmaceutical biotechnology have paved the way to ground-breaking new biological therapeutic modalities, offering the possibility of a durable curative approach for a number of life-threatening diseases, for which the medical need is as yet unmet. Over the past decades, gene therapy has seen a massive transformation from a proof-of-concept approach to a clinical reality culminating in the regulatory approval of state-of-the-art products in the European Union and in the United States. This book captures some of the scientific progresses notably in gene transfer technologies and translational development of in vivo and ex vivo gene therapy interventions in the treatment of a broad range of complex and debilitating non-inherited and inherited disorders such as: human immunodeficiency virus 1 (HIV-1) infection, cancer, cystic fibrosis, hereditary retinopathies, haemophilia B, cardiac diseases, and chronic liver fibrosis.

Description
Summary:	Ongoing advances in pharmaceutical biotechnology have paved the way to ground-breaking new biological therapeutic modalities, offering the possibility of a durable curative approach for a number of life-threatening diseases, for which the medical need is as yet unmet. Over the past decades, gene therapy has seen a massive transformation from a proof-of-concept approach to a clinical reality culminating in the regulatory approval of state-of-the-art products in the European Union and in the United States. This book captures some of the scientific progresses notably in gene transfer technologies and translational development of in vivo and ex vivo gene therapy interventions in the treatment of a broad range of complex and debilitating non-inherited and inherited disorders such as: human immunodeficiency virus 1 (HIV-1) infection, cancer, cystic fibrosis, hereditary retinopathies, haemophilia B, cardiac diseases, and chronic liver fibrosis.
Physical Description:	1 online resource
ISBN:	9781789857177 1789857171 9781789857184 178985718X 9781839620829 183962082X